PT Inquest is an online journal club. Hosted by Jason Tuori, Megan Graham, and Chris Juneau, the show looks at an article every week and discusses how it applies to current physical therapy practice.
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Вміст надано NeurologyLive® Mind Moments®. Весь вміст подкастів, включаючи епізоди, графіку та описи подкастів, завантажується та надається безпосередньо компанією NeurologyLive® Mind Moments® або його партнером по платформі подкастів. Якщо ви вважаєте, що хтось використовує ваш захищений авторським правом твір без вашого дозволу, ви можете виконати процедуру, описану тут https://uk.player.fm/legal.
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80: Advancing Treatment for Rare Neuromuscular Disorders
MP3•Головна епізоду
Manage episode 352422139 series 3340456
Вміст надано NeurologyLive® Mind Moments®. Весь вміст подкастів, включаючи епізоди, графіку та описи подкастів, завантажується та надається безпосередньо компанією NeurologyLive® Mind Moments® або його партнером по платформі подкастів. Якщо ви вважаєте, що хтось використовує ваш захищений авторським правом твір без вашого дозволу, ви можете виконати процедуру, описану тут https://uk.player.fm/legal.
Welcome to the NeurologyLive® Mind Moments® podcast. Tune in to hear leaders in neurology sound off on topics that impact your clinical practice.
In this episode, we spoke with Sarah Boyce, president and CEO of Avidity Biosciences, who shared insight into the company's ongoing work with its antibody oligonucleotide conjugates (AOC) platform and the focus on myotonic dystrophy type 1 (DM1), Duchenne muscular dystrophy (DMD), and facioscapulohumeral muscular dystrophy (FSHD) treatments, as well as the challenges with developing successful RNA therapies, and more.
Looking for more neuromuscular disorder discussion? Check out the NeurologyLive® neuromuscular clinical focus page: neurologylive.com/clinical/neuromuscular
Episode Breakdown:
In this episode, we spoke with Sarah Boyce, president and CEO of Avidity Biosciences, who shared insight into the company's ongoing work with its antibody oligonucleotide conjugates (AOC) platform and the focus on myotonic dystrophy type 1 (DM1), Duchenne muscular dystrophy (DMD), and facioscapulohumeral muscular dystrophy (FSHD) treatments, as well as the challenges with developing successful RNA therapies, and more.
Looking for more neuromuscular disorder discussion? Check out the NeurologyLive® neuromuscular clinical focus page: neurologylive.com/clinical/neuromuscular
Episode Breakdown:
- 1:20 – Current limitations with RNA therapies
- 4:50 – The decision to focus on rare genetic muscle diseases
- 7:45 – The patient needs in DM1, FSHD, and DMD
- 9:05 – Neurology News Minute
- 12:25 – Other clinical areas of focus and collaboration for Avidity
- 14:10 – Upcoming data presentations planned for 2023 in DMD and myotonic dystrophy
- 16:15 – The benefits of collaboration in the rare disease community
- 18:15 – Looking ahead to the future of therapies in rare muscular disease
This episode is brought to you by the Giants of Multiple Sclerosis®. This premier neuroscience award program celebrates pioneers, innovators, and future generations of leaders for their remarkable achievements in Multiple Sclerosis. Nominations close January 31, 2023!
Nominate: neurologylive.com/Giants-of-MS
The stories featured in this week's Neurology News Minute, which will give you quick updates on the following developments in neurology, are further detailed here:
- Anti-CD20 Therapy Ublituximab Gains FDA Approval for Relapsing Multiple Sclerosis
- FDA Clears First Stroke-Specific Radial Access Platform for Mechanical Thrombectomy
- FDA Designates Myasthenia Gravis Agent Rozanolixizumab Application for Priority Review
- FDA Approves Eisai’s Lecanemab for the Treatment for Alzheimer Disease
- FDA Accepts sBLA for Revance’s Cervical Dystonia Treatment DaxibotulinumtoxinA
Thanks for listening to the NeurologyLive® Mind Moments® podcast. To support the show, be sure to rate, review, and subscribe wherever you listen to podcasts. For more neurology news and expert-driven content, visit neurologylive.com.
126 епізодів
MP3•Головна епізоду
Manage episode 352422139 series 3340456
Вміст надано NeurologyLive® Mind Moments®. Весь вміст подкастів, включаючи епізоди, графіку та описи подкастів, завантажується та надається безпосередньо компанією NeurologyLive® Mind Moments® або його партнером по платформі подкастів. Якщо ви вважаєте, що хтось використовує ваш захищений авторським правом твір без вашого дозволу, ви можете виконати процедуру, описану тут https://uk.player.fm/legal.
Welcome to the NeurologyLive® Mind Moments® podcast. Tune in to hear leaders in neurology sound off on topics that impact your clinical practice.
In this episode, we spoke with Sarah Boyce, president and CEO of Avidity Biosciences, who shared insight into the company's ongoing work with its antibody oligonucleotide conjugates (AOC) platform and the focus on myotonic dystrophy type 1 (DM1), Duchenne muscular dystrophy (DMD), and facioscapulohumeral muscular dystrophy (FSHD) treatments, as well as the challenges with developing successful RNA therapies, and more.
Looking for more neuromuscular disorder discussion? Check out the NeurologyLive® neuromuscular clinical focus page: neurologylive.com/clinical/neuromuscular
Episode Breakdown:
In this episode, we spoke with Sarah Boyce, president and CEO of Avidity Biosciences, who shared insight into the company's ongoing work with its antibody oligonucleotide conjugates (AOC) platform and the focus on myotonic dystrophy type 1 (DM1), Duchenne muscular dystrophy (DMD), and facioscapulohumeral muscular dystrophy (FSHD) treatments, as well as the challenges with developing successful RNA therapies, and more.
Looking for more neuromuscular disorder discussion? Check out the NeurologyLive® neuromuscular clinical focus page: neurologylive.com/clinical/neuromuscular
Episode Breakdown:
- 1:20 – Current limitations with RNA therapies
- 4:50 – The decision to focus on rare genetic muscle diseases
- 7:45 – The patient needs in DM1, FSHD, and DMD
- 9:05 – Neurology News Minute
- 12:25 – Other clinical areas of focus and collaboration for Avidity
- 14:10 – Upcoming data presentations planned for 2023 in DMD and myotonic dystrophy
- 16:15 – The benefits of collaboration in the rare disease community
- 18:15 – Looking ahead to the future of therapies in rare muscular disease
This episode is brought to you by the Giants of Multiple Sclerosis®. This premier neuroscience award program celebrates pioneers, innovators, and future generations of leaders for their remarkable achievements in Multiple Sclerosis. Nominations close January 31, 2023!
Nominate: neurologylive.com/Giants-of-MS
The stories featured in this week's Neurology News Minute, which will give you quick updates on the following developments in neurology, are further detailed here:
- Anti-CD20 Therapy Ublituximab Gains FDA Approval for Relapsing Multiple Sclerosis
- FDA Clears First Stroke-Specific Radial Access Platform for Mechanical Thrombectomy
- FDA Designates Myasthenia Gravis Agent Rozanolixizumab Application for Priority Review
- FDA Approves Eisai’s Lecanemab for the Treatment for Alzheimer Disease
- FDA Accepts sBLA for Revance’s Cervical Dystonia Treatment DaxibotulinumtoxinA
Thanks for listening to the NeurologyLive® Mind Moments® podcast. To support the show, be sure to rate, review, and subscribe wherever you listen to podcasts. For more neurology news and expert-driven content, visit neurologylive.com.
126 епізодів
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